预计罕见病治疗市场在 2024 年至 2031 年期间的复合年增长率为 9.3%,市场规模将从 2024 年的 XX 百万美元扩大到 2031 年的 XX 百万美元。
报告按治疗领域(肿瘤、神经系统疾病、心血管疾病、肌肉骨骼疾病、传染病、其他)、给药途径(口服、注射和其他)、药物类型(生物制剂、小分子和生物仿制药)和分销渠道(网上药店、专科药店和医院药店)进行细分,
全球分析进一步细分为区域和主要国家。报告以美元为单位提供上述分析和细分的价值。
报告目的
The Insight Partners 发布的《罕见病治疗市场》报告旨在描述当前形势和未来增长、主要驱动因素、挑战和机遇。这将为各种业务利益相关者提供见解,例如:
- 技术提供商/制造商:了解不断变化的市场动态并了解潜在的增长机会,从而能够做出明智的战略决策。
- 投资者:对市场增长率、市场财务预测以及整个价值链中存在的机会进行全面的趋势分析。
- 监管机构:监管市场政策和警察活动,旨在最大限度地减少滥用行为,维护投资者的信任和信心,维护市场的完整性和稳定性。
罕见病治疗市场细分
治疗领域
- 肿瘤学
- 神经系统疾病
- 心血管疾病
- 肌肉骨骼疾病
- 传染病
- 其他的
给药途径
- 口服
- 注射剂及其他
药物类型
- 生物制剂
- 小分子和生物仿制药
分销渠道
- 网上药店
- 专业药房和医院药房
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- 获取此报告的关键市场趋势。这个免费样品将包括数据分析,从市场趋势到估计和预测。
罕见病治疗市场增长动力
- 随着罕见病发病率的不断上升,治疗方法也越来越多:医疗保健中发现罕见病的成功率提高了患者的诊断率,从而继续扩大了专科治疗市场。其中,遗传学、自身免疫和需要特殊治疗的神经系统疾病是其中的佼佼者。
- 技术进步:生物技术和基因编辑技术(例如 CRISPR 技术)的进步改变了罕见病的治疗方法。高级个人治疗本质上是一种针对遗传疾病原因的基因治疗,它推动了更先进的治疗方法。制药公司和投资者响应这一需求,因此增加了罕见病治疗的市场规模。
- 政府对孤儿药的政策和激励措施:世界各国政府正在制定立法,鼓励开发治疗罕见疾病的药物。在美国,税收减免、市场独占权和补助金是《孤儿药法案》下的激励措施,可给予开发治疗罕见疾病药物的公司。其他地区和欧盟的计划使对罕见疾病药物的投资更加有利可图
罕见病治疗市场未来趋势
- 投资数量不断增加:在罕见病治疗领域,对基因和细胞疗法的投资数量不断增加,这一领域将继续增长,尤其是在囊性纤维化或杜氏肌营养不良症等遗传疾病方面。就基因和细胞疗法而言,通过解决这些疾病的遗传原因,有可能治愈或长期管理这些疾病。这是在罕见病领域观察到的一个特殊趋势。
- 精准医疗的兴起:如今,精准医疗已成为罕见病治疗领域最新的决定性趋势之一。随着基因组学的革命,尤其是生物标志物的识别,针对基因图谱的治疗可以代表有效且有针对性的疗法,尤其是针对罕见和复杂的疾病,从而实现更好的患者治疗效果,并减少药物的副作用,因为精准治疗可以针对特定的基因突变。
- 合作与伙伴关系的进步:制药公司与学术界、生物技术公司和患者权益组织合作,寻找罕见病的潜在新疗法。在这方面,这种合作共享资源和专业知识,以加快新疗法的开发。此外,这些合作模式将在继续实施公私合作安排的罕见病领域蓬勃发展。
罕见病治疗市场机会
- 进入尚未得到满足的罕见疾病领域:罕见疾病是医药公司可以重点关注的广阔领域,因为大多数此类疾病没有有效的治疗方法或疗效有限。公司可以将注意力集中在罕见癌症、神经肌肉疾病和罕见代谢紊乱等领域的未满足需求,以填补当前疗法的空白,并开拓利润丰厚但对创新疗法需求旺盛的小众市场。
- 新兴市场为罕见病治疗带来新机遇:随着新兴市场医疗保健服务优势的日益明显,亚太、拉丁美洲和中东等地区对罕见病治疗的需求正在上升。由于人们对新疗法的认识和诊断能力不断提高,公司在考虑进军这些地区方面拥有巨大的机遇。
- 联合疗法的设计:由于大多数罕见病都很复杂,因此可能需要多方面的治疗过程。这将为设计联合疗法提供一个机会,这种疗法可以同时从多个方面影响罕见病并增强治疗效果。这非常适用于罕见癌症、自身免疫性疾病和遗传性疾病等需要采用多种药物治疗的疾病。
罕见病治疗市场区域洞察
Insight Partners 的分析师已详尽解释了预测期内影响罕见病治疗市场的区域趋势和因素。本节还讨论了北美、欧洲、亚太地区、中东和非洲以及南美和中美洲的罕见病治疗市场细分和地理位置。
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- 获取罕见病治疗市场的区域特定数据
罕见病治疗市场报告范围
报告属性 | 细节 |
---|---|
2024 年的市场规模 | XX 百万美元 |
2031 年市场规模 | XX 百万美元 |
全球复合年增长率(2025 - 2031) | 9.3% |
史料 | 2021-2023 |
预测期 | 2025-2031 |
涵盖的领域 | 按治疗领域
|
覆盖地区和国家 | 北美
|
市场领导者和主要公司简介 |
|
罕见病治疗市场参与者密度:了解其对业务动态的影响
罕见病治疗市场正在快速增长,这得益于终端用户需求的不断增长,而这些需求又源于消费者偏好的不断变化、技术进步以及对产品优势的认识不断提高等因素。随着需求的增加,企业正在扩大其产品范围,进行创新以满足消费者的需求,并利用新兴趋势,从而进一步推动市场增长。
市场参与者密度是指在特定市场或行业内运营的企业或公司的分布情况。它表明在给定市场空间中,相对于其规模或总市场价值,有多少竞争对手(市场参与者)存在。
在罕见病治疗市场运营的主要公司有:
- F.霍夫曼-罗氏有限公司
- 辉瑞公司
- PTC 治疗公司
- 诺华公司
- 武田药品工业公司
免责声明:上面列出的公司没有按照任何特定顺序排列。
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- 了解罕见病治疗市场顶级关键参与者概况
主要卖点
- 全面覆盖:报告全面涵盖了罕见疾病治疗市场的产品、服务、类型和最终用户的分析,提供了整体概况。
- 专家分析:报告基于对行业专家和分析师的深入了解而编写。
- 最新信息:该报告涵盖了最新信息和数据趋势,确保了其与业务的相关性。
- 定制选项:此报告可以定制以满足特定客户要求并恰当地适应业务策略。
因此,罕见病治疗市场研究报告有助于引领解读和了解行业情景和增长前景。尽管可能存在一些合理的担忧,但本报告的总体优势往往大于劣势。
- 历史分析(2 年)、基准年、预测(7 年)及复合年增长率
- PEST 和 SWOT 分析
- 市场规模价值/数量 - 全球、区域、国家
- 行业和竞争格局
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Report Coverage
Revenue forecast, Company Analysis, Industry landscape, Growth factors, and Trends
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Segment Covered
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to segments covered.
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Regional Scope
North America, Europe, Asia Pacific, Middle East & Africa, South & Central America
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Country Scope
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常见问题
F. Hoffmann-La Roche Ltd., Pfizer, Inc., PTC Therapeutics, Novartis AG, Takeda Pharmaceutical Company, Bayer AG, AbbVie Inc., Merck & Co. Inc., and Bristol Myers Squibb
The market is expected to grow at a CAGR of 10.2%
The Rare Disease Treatment Market is estimated to witness a CAGR of 9.3% from 2023 to 2031
Asia Pacific region dominated the Rare Disease Treatment Market in 2023
North America region dominated the Rare Disease Treatment Market in 2023
Asia Pacific is estimated to grow at the highest CAGR over the forecast year (2023: 2031)
Trends and growth analysis reports related to Life Sciences : READ MORE..
- F. Hoffmann-La Roche Ltd.
- Pfizer, Inc.
- PTC Therapeutics
- Novartis AG
- Takeda Pharmaceutical Company
- Bayer AG
- AbbVie Inc.
- Merck & Co. Inc.
- Bristol Myers Squibb
The Insight Partners performs research in 4 major stages: Data Collection & Secondary Research, Primary Research, Data Analysis and Data Triangulation & Final Review.
- Data Collection and Secondary Research:
As a market research and consulting firm operating from a decade, we have published and advised several client across the globe. First step for any study will start with an assessment of currently available data and insights from existing reports. Further, historical and current market information is collected from Investor Presentations, Annual Reports, SEC Filings, etc., and other information related to company’s performance and market positioning are gathered from Paid Databases (Factiva, Hoovers, and Reuters) and various other publications available in public domain.
Several associations trade associates, technical forums, institutes, societies and organization are accessed to gain technical as well as market related insights through their publications such as research papers, blogs and press releases related to the studies are referred to get cues about the market. Further, white papers, journals, magazines, and other news articles published in last 3 years are scrutinized and analyzed to understand the current market trends.
- Primary Research:
The primarily interview analysis comprise of data obtained from industry participants interview and answers to survey questions gathered by in-house primary team.
For primary research, interviews are conducted with industry experts/CEOs/Marketing Managers/VPs/Subject Matter Experts from both demand and supply side to get a 360-degree view of the market. The primary team conducts several interviews based on the complexity of the markets to understand the various market trends and dynamics which makes research more credible and precise.
A typical research interview fulfils the following functions:
- Provides first-hand information on the market size, market trends, growth trends, competitive landscape, and outlook
- Validates and strengthens in-house secondary research findings
- Develops the analysis team’s expertise and market understanding
Primary research involves email interactions and telephone interviews for each market, category, segment, and sub-segment across geographies. The participants who typically take part in such a process include, but are not limited to:
- Industry participants: VPs, business development managers, market intelligence managers and national sales managers
- Outside experts: Valuation experts, research analysts and key opinion leaders specializing in the electronics and semiconductor industry.
Below is the breakup of our primary respondents by company, designation, and region:
Once we receive the confirmation from primary research sources or primary respondents, we finalize the base year market estimation and forecast the data as per the macroeconomic and microeconomic factors assessed during data collection.
- Data Analysis:
Once data is validated through both secondary as well as primary respondents, we finalize the market estimations by hypothesis formulation and factor analysis at regional and country level.
- Macro-Economic Factor Analysis:
We analyse macroeconomic indicators such the gross domestic product (GDP), increase in the demand for goods and services across industries, technological advancement, regional economic growth, governmental policies, the influence of COVID-19, PEST analysis, and other aspects. This analysis aids in setting benchmarks for various nations/regions and approximating market splits. Additionally, the general trend of the aforementioned components aid in determining the market's development possibilities.
- Country Level Data:
Various factors that are especially aligned to the country are taken into account to determine the market size for a certain area and country, including the presence of vendors, such as headquarters and offices, the country's GDP, demand patterns, and industry growth. To comprehend the market dynamics for the nation, a number of growth variables, inhibitors, application areas, and current market trends are researched. The aforementioned elements aid in determining the country's overall market's growth potential.
- Company Profile:
The “Table of Contents” is formulated by listing and analyzing more than 25 - 30 companies operating in the market ecosystem across geographies. However, we profile only 10 companies as a standard practice in our syndicate reports. These 10 companies comprise leading, emerging, and regional players. Nonetheless, our analysis is not restricted to the 10 listed companies, we also analyze other companies present in the market to develop a holistic view and understand the prevailing trends. The “Company Profiles” section in the report covers key facts, business description, products & services, financial information, SWOT analysis, and key developments. The financial information presented is extracted from the annual reports and official documents of the publicly listed companies. Upon collecting the information for the sections of respective companies, we verify them via various primary sources and then compile the data in respective company profiles. The company level information helps us in deriving the base number as well as in forecasting the market size.
- Developing Base Number:
Aggregation of sales statistics (2020-2022) and macro-economic factor, and other secondary and primary research insights are utilized to arrive at base number and related market shares for 2022. The data gaps are identified in this step and relevant market data is analyzed, collected from paid primary interviews or databases. On finalizing the base year market size, forecasts are developed on the basis of macro-economic, industry and market growth factors and company level analysis.
- Data Triangulation and Final Review:
The market findings and base year market size calculations are validated from supply as well as demand side. Demand side validations are based on macro-economic factor analysis and benchmarks for respective regions and countries. In case of supply side validations, revenues of major companies are estimated (in case not available) based on industry benchmark, approximate number of employees, product portfolio, and primary interviews revenues are gathered. Further revenue from target product/service segment is assessed to avoid overshooting of market statistics. In case of heavy deviations between supply and demand side values, all thes steps are repeated to achieve synchronization.
We follow an iterative model, wherein we share our research findings with Subject Matter Experts (SME’s) and Key Opinion Leaders (KOLs) until consensus view of the market is not formulated – this model negates any drastic deviation in the opinions of experts. Only validated and universally acceptable research findings are quoted in our reports.
We have important check points that we use to validate our research findings – which we call – data triangulation, where we validate the information, we generate from secondary sources with primary interviews and then we re-validate with our internal data bases and Subject matter experts. This comprehensive model enables us to deliver high quality, reliable data in shortest possible time.